Antisense oligonucleotide treatment has therapeutic potential in a severe form of Charcot–Marie–Tooth disease, according to a new study.

中文翻译：

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反义寡核苷酸在夏科-玛丽-图思病中显示出潜力


一项新的研究表明，反义寡核苷酸治疗对于严重的腓骨肌萎缩症具有治疗潜力。